Ophthalmology Times
September 10, 2026
Ophthalmology Times reports on early clinical trial results that show the investigational gene therapy OPGx-BEST1 improved vision and retinal structure in patients with rare inherited retinal diseases, with no serious safety concerns reported. Mark Pennesi, M.D., Ph.D., says, “We are encouraged by the localization of functional gains to areas of viable, compromised retina and by the opportunity to apply these insights prospectively as OPGx-BEST1 is advanced into cohort 2 and potential pivotal development.”