OHSU gene editing procedure partially restores vision
May 06, 2024
A Phase I/II clinical trial finds that a CRISPR-based gene editing technology improved vision in 11 of 14 participants who were born with a blindness-causing gene mutation. Mark Pennesi, M.D., Ph.D., says, “As ophthalmologists, we were often taught that there aren't really treatments for these rare genetic diseases. That is changing."